Joseph ShavitJan 4, 2023Breakthrough gene therapy saved a child from “Bubble Boy Disease”HT had a rare mutation in the DCLRE1C or Artemis gene, meaning he had Artemis-SCID – the most serious of primary immunodeficiencies.
Joseph ShavitSep 7, 2022Single stem cell-gene therapy session can treat ALS for 3 years, study findsUsing stem cells is a powerful way to deliver important proteins to the brain or spinal cord that can’t get through the blood-brain barrier.
Joseph ShavitMar 28, 2022Opioid-free solution for chronic pain developed by scientistsA gene therapy for chronic pain, developed by researchers at UC San Diego, could offer a safer, non-addictive alternative to opioids.
Joseph ShavitFeb 24, 2022'First-of-its-kind' gene therapy restores severe hearing lossHearing loss has been linked to mutations in at least 100 different genes, but up to 16 percent can be traced to just one gene, STRC.
Joseph ShavitDec 16, 2021Gene therapy advance shown to restore severe hearing lossHearing loss has been linked to mutations in ~100 different genes, but up to 16 percent of genetic hearing loss can be traced to STRC gene.
Joseph ShavitOct 19, 2021Gene therapy can restore vision after strokeMost strokes happen when an artery in the brain becomes blocked. Blood flow to the neural tissue stops, and those tissues typically die.
Joseph ShavitMay 25, 2021A new type of gene-based therapy partially restored a blind man’s visionLight-activated proteins inserted in eye nerve cells and special goggles help him see objects
Joseph ShavitMar 11, 2021With gene therapy, scientists develop opioid-free solution for chronic painA gene therapy for chronic pain could offer a safer, non-addictive alternative to opioids. Researchers at the UCSD...